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Vivo-Morpholinos in primary human fibroblasts

Jon Moulton

Thursday, 29 Oct 2009 18:00 UTC

Vivo-Morpholinos used in primary human fibroblasts, also unmodified Morpholinos delivered using Endo-Porter in similar cultures.

Pérez B, Rincón A, Jorge-Finnigan A, Richard E, Merinero B, Ugarte M, Desviat LR. Pseudoexon exclusion by antisense therapy in methylmalonic aciduria (MMAuria). Hum Mutat. 2009 Sep 2. [Epub ahead of print]


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