Vivo-Morpholinos in primary human fibroblasts
Jon Moulton
Thursday, 29 October 2009 18:00 UTC
Vivo-Morpholinos used in primary human fibroblasts, also unmodified Morpholinos delivered using Endo-Porter in similar cultures.
Pérez B, Rincón A, Jorge-Finnigan A, Richard E, Merinero B, Ugarte M, Desviat LR. Pseudoexon exclusion by antisense therapy in methylmalonic aciduria (MMAuria). Hum Mutat. 2009 Sep 2. [Epub ahead of print]
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