Morpholino oligos forum: topic

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Endo-Porter used to deliver Morpholinos into human primary fibroblasts

Jon Moulton

Tuesday, 15 Sep 2009 17:45 UTC

Rodríguez-Pascau L, Coll MJ, Vilageliu L, Grinberg D. Antisense oligonucleotide treatment for a pseudoexon-generating mutation in the NPC1 gene causing Niemann-Pick type C disease. Hum Mutat. 2009 Aug 30. [Epub ahead of print]

Updated 15 Sep 2009 17:46 UTC


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