Morpholino oligos forum: topic

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New peptide-Morpholino conjugates for Duchenne muscular dystrophy

Jon Moulton

Tuesday, 15 Sep 2009 15:15 UTC

New modifications of arginine-rich cell penetrating peptides delivering Morpholino oligos in mdx mice:

Yin H, Moulton HM, Betts C, Seow Y, Boutilier J, Iverson PL, Wood MJ. A fusion peptide directs enhanced systemic dystrophin exon skipping and functional restoration in dystrophin-deficient mdx mice. Hum Mol Genet. 2009 Aug 18. [Epub ahead of print]


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