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Beta-thalassemia treated in mice with splice-modifying Morpholino
Posted by:
Jon Moulton
Tags:
morpholino
mouse
thalassemia
splice
mutation
0 replies
Vivo-Morpholinos in primary human fibroblasts
Posted by:
Jon Moulton
Tags:
vivo-morpholino
morpholino
endo-porter
fibroblast
human
mutation
methylmalonic
aciduria
0 replies
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